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A Duchenne Muscular Dystrophy Gene Hot Spot Mutation in Dystrophin-Deficient Cavalier King Charles Spaniels Is Amenable to Exon 51 Skipping
- Gemma L. Walmsley,
- Virginia Arechavala-Gomeza,
- Marta Fernandez-Fuente,
- Margaret M. Burke,
- Nicole Nagel,
- Angela Holder,
- Rachael Stanley,
- Kate Chandler,
- Stanley L. Marks,
- Francesco Muntoni
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- Published: January 13, 2010
- https://doi.org/10.1371/journal.pone.0008647