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Chronic Cyclodextrin Treatment of Murine Niemann-Pick C Disease Ameliorates Neuronal Cholesterol and Glycosphingolipid Storage and Disease Progression
- Cristin D. Davidson,
- Nafeeza F. Ali,
- Matthew C. Micsenyi,
- Gloria Stephney,
- Sophie Renault,
- Kostantin Dobrenis,
- Daniel S. Ory,
- Marie T. Vanier,
- Steven U. Walkley
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- Published: September 11, 2009
- https://doi.org/10.1371/journal.pone.0006951