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Development of a Single Vector System that Enhances Trans-Splicing of SMN2 Transcripts

  • Tristan H. Coady,

    Affiliation Department of Veterinary Pathobiology, Bond Life Sciences Center, University of Missouri, Columbia, Missouri, United States of America

  • Travis D. Baughan,

    Affiliation Department of Molecular Microbiology and Immunology, Bond Life Sciences Center, University of Missouri, Columbia, Missouri, United States of America

  • Monir Shababi,

    Affiliation Department of Veterinary Pathobiology, Bond Life Sciences Center, University of Missouri, Columbia, Missouri, United States of America

  • Marco A. Passini,

    Affiliation Neuroscience, Genzyme Corporation, Framingham, Massachusetts, United States of America

  • Christian L. Lorson

    lorsonc@missouri.edu

    Affiliations Department of Veterinary Pathobiology, Bond Life Sciences Center, University of Missouri, Columbia, Missouri, United States of America, Department of Molecular Microbiology and Immunology, Bond Life Sciences Center, University of Missouri, Columbia, Missouri, United States of America

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