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HDAC Inhibitors Correct Frataxin Deficiency in a Friedreich Ataxia Mouse Model

  • Myriam Rai,

    Affiliation Laboratoire de Neurologie Expérimentale, Hôpital Erasme, Université Libre de Bruxelles (ULB), Brussels, Belgium

  • Elisabetta Soragni,

    Affiliation Department of Molecular Biology, The Scripps Research Institute, La Jolla, California, United States of America

  • Kai Jenssen,

    Current address: Merz Pharmaceutical GmbH, Frankfurt am Main, Germany

    Affiliation Department of Molecular Biology, The Scripps Research Institute, La Jolla, California, United States of America

  • Ryan Burnett,

    Affiliation Department of Molecular Biology, The Scripps Research Institute, La Jolla, California, United States of America

  • David Herman,

    Affiliation Department of Molecular Biology, The Scripps Research Institute, La Jolla, California, United States of America

  • Giovanni Coppola,

    Affiliation Program in Neurogenetics, Department of Neurology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

  • Daniel H. Geschwind,

    Affiliation Program in Neurogenetics, Department of Neurology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

  • Joel M. Gottesfeld,

    Affiliation Department of Molecular Biology, The Scripps Research Institute, La Jolla, California, United States of America

  • Massimo Pandolfo

    massimo.pandolfo@ulb.ac.be

    Affiliation Laboratoire de Neurologie Expérimentale, Hôpital Erasme, Université Libre de Bruxelles (ULB), Brussels, Belgium

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