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High-Efficiency Transduction of Primary Human Hematopoietic Stem Cells and Erythroid Lineage-Restricted Expression by Optimized AAV6 Serotype Vectors In Vitro and in a Murine Xenograft Model In Vivo

  • Liujiang Song,

    Affiliations Experimental Hematology Laboratory, Department of Physiology, School of Basic Medical Sciences, Central South University, Changsha, China, Shenzhen Institute of Xiangya Biomedicine, Shenzhen, China, Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida College of Medicine, Gainesville, Florida, United States of America, Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, Florida, United States of America, Genetics Institute, University of Florida College of Medicine, Gainesville, Florida, United States of America

  • Xiaomiao Li,

    Affiliations Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida College of Medicine, Gainesville, Florida, United States of America, Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, Florida, United States of America, Genetics Institute, University of Florida College of Medicine, Gainesville, Florida, United States of America

  • Giridhara R. Jayandharan,

    Affiliations Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida College of Medicine, Gainesville, Florida, United States of America, Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, Florida, United States of America, Genetics Institute, University of Florida College of Medicine, Gainesville, Florida, United States of America, Department of Haematology, Christian Medical College, Vellore, Tamil Nadu, India, Center for Stem Cell Research, Christian Medical College, Vellore, Tamil Nadu, India

  • Yuan Wang,

    Affiliations Department of Traditional Chinese Medicine, Changhai Hospital, Second Military Medical University, Shanghai, China, Shanghai University of Traditional Chinese Medicine, Shanghai, China

  • George V. Aslanidi,

    Affiliations Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida College of Medicine, Gainesville, Florida, United States of America, Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, Florida, United States of America, Genetics Institute, University of Florida College of Medicine, Gainesville, Florida, United States of America

  • Chen Ling,

    Affiliations Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida College of Medicine, Gainesville, Florida, United States of America, Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, Florida, United States of America, Genetics Institute, University of Florida College of Medicine, Gainesville, Florida, United States of America

  • Li Zhong,

    Affiliations Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida College of Medicine, Gainesville, Florida, United States of America, Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, Florida, United States of America, Genetics Institute, University of Florida College of Medicine, Gainesville, Florida, United States of America, Gene Therapy Center, University of Massachusetts Medical School, Worcester, Massachusetts, United States of America, Department of Pediatrics, University of Massachusetts Medical School, Worcester, Massachusetts, United States of America

  • Guangping Gao,

    Affiliations Gene Therapy Center, University of Massachusetts Medical School, Worcester, Massachusetts, United States of America, Department of Microbiology & Physiology Systems, University of Massachusetts Medical School, Worcester, Massachusetts, United States of America

  • Mervin C. Yoder,

    Affiliations Herman B Well Center for Pediatric Research, Indiana University School of Medicine, Indianapolis, Indiana, United States of America, Department of Pediatrics, Indiana University School of Medicine, Indianapolis, Indiana, United States of America

  • Changquan Ling,

    Affiliations Department of Traditional Chinese Medicine, Changhai Hospital, Second Military Medical University, Shanghai, China, Shanghai University of Traditional Chinese Medicine, Shanghai, China

  • Mengqun Tan ,

    mqtan26@163.com (MT); aruns@peds.ufl.edu (AS)

    Affiliations Experimental Hematology Laboratory, Department of Physiology, School of Basic Medical Sciences, Central South University, Changsha, China, Shenzhen Institute of Xiangya Biomedicine, Shenzhen, China

  • Arun Srivastava

    mqtan26@163.com (MT); aruns@peds.ufl.edu (AS)

    Affiliations Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida College of Medicine, Gainesville, Florida, United States of America, Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, Florida, United States of America, Genetics Institute, University of Florida College of Medicine, Gainesville, Florida, United States of America, Department of Molecular Genetics and Microbiology, University of Florida College of Medicine, Gainesville, Florida, United States of America, Shands Cancer Center, University of Florida College of Medicine, Gainesville, Florida, United States of America

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