Pharmacological Screening Using an FXN-EGFP Cellular Genomic Reporter Assay for the Therapy of Friedreich Ataxia

• Lingli Li,

  Affiliations Cell and Gene Therapy, Murdoch Childrens Research Institute, Parkville, Victoria, Australia, Bruce Lefroy Centre for Genetic Health Research, Murdoch Childrens Research Institute, Parkville, Victoria, Australia

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• Lucille Voullaire,

  Affiliation Cell and Gene Therapy, Murdoch Childrens Research Institute, Parkville, Victoria, Australia

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• Chiranjeevi Sandi,

  Affiliation Division of Biosciences, School of Health Sciences and Social Care, Brunel University, Uxbridge, United Kingdom

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• Mark A. Pook,

  Affiliation Division of Biosciences, School of Health Sciences and Social Care, Brunel University, Uxbridge, United Kingdom

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• Panos A. Ioannou ,

  Contributed equally to this work with: Panos A. Ioannou, Martin B. Delatycki, Joseph P. Sarsero

  ¶† Deceased

  Affiliations Cell and Gene Therapy, Murdoch Childrens Research Institute, Parkville, Victoria, Australia, Department of Paediatrics, The University of Melbourne, Royal Children’s Hospital, Parkville, Victoria, Australia

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• Martin B. Delatycki ,

  Contributed equally to this work with: Panos A. Ioannou, Martin B. Delatycki, Joseph P. Sarsero

  Affiliations Bruce Lefroy Centre for Genetic Health Research, Murdoch Childrens Research Institute, Parkville, Victoria, Australia, Department of Paediatrics, The University of Melbourne, Royal Children’s Hospital, Parkville, Victoria, Australia, Department of Clinical Genetics, Austin Health, Heidelberg, Victoria, Australia

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• Joseph P. Sarsero

  Contributed equally to this work with: Panos A. Ioannou, Martin B. Delatycki, Joseph P. Sarsero

  * E-mail: joe@sarsero.com

  Affiliations Cell and Gene Therapy, Murdoch Childrens Research Institute, Parkville, Victoria, Australia, Bruce Lefroy Centre for Genetic Health Research, Murdoch Childrens Research Institute, Parkville, Victoria, Australia, Department of Paediatrics, The University of Melbourne, Royal Children’s Hospital, Parkville, Victoria, Australia

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