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Homologous Recombination Mediates Functional Recovery of Dysferlin Deficiency following AAV5 Gene Transfer
- William E. Grose,
- K. Reed Clark,
- Danielle Griffin,
- Vinod Malik,
- Kimberly M. Shontz,
- Chrystal L. Montgomery,
- Sarah Lewis,
- Robert H. Brown Jr.,
- Paul M. L. Janssen,
- Jerry R. Mendell
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- Published: June 15, 2012
- https://doi.org/10.1371/journal.pone.0039233
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