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SMA CARNI-VAL TRIAL PART II: A Prospective, Single-Armed Trial of L-Carnitine and Valproic Acid in Ambulatory Children with Spinal Muscular Atrophy
- John T. Kissel,
- Charles B. Scott,
- Sandra P. Reyna,
- Thomas O. Crawford,
- Louise R. Simard,
- Kristin J. Krosschell,
- Gyula Acsadi,
- Bakri Elsheik,
- Mary K. Schroth,
- Guy D'Anjou
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- Published: July 6, 2011
- https://doi.org/10.1371/journal.pone.0021296