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Leber Congenital Amaurosis Associated with AIPL1: Challenges in Ascribing Disease Causation, Clinical Findings, and Implications for Gene Therapy
Tan MH,
Mackay DS,
Cowing J,
Tran HV,
Smith AJ,
et al.
(2012)
Leber Congenital Amaurosis Associated with AIPL1: Challenges in Ascribing Disease Causation, Clinical Findings, and Implications for Gene Therapy.
PLOS ONE 7(3): e32330.
https://doi.org/10.1371/journal.pone.0032330