Download Citation
Article Source:
AAV-Mediated Gene Delivery in Adult GM1-Gangliosidosis Mice Corrects Lysosomal Storage in CNS and Improves Survival
Baek RC,
Broekman MLD,
Leroy SG,
Tierney LA,
Sandberg MA,
et al.
(2010)
AAV-Mediated Gene Delivery in Adult GM1-Gangliosidosis Mice Corrects Lysosomal Storage in CNS and Improves Survival.
PLOS ONE 5(10): e13468.
https://doi.org/10.1371/journal.pone.0013468