About the Authors
- John P. Clancy
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* E-mail: john.clancy@cchmc.org
Affiliation Department of Pediatrics, Cincinnati Children’s Hospital Medical Center and the University of Cincinnati, Cincinnati, Ohio, United States of America
- Rhonda D. Szczesniak
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Affiliation Department of Pediatrics, Cincinnati Children’s Hospital Medical Center and the University of Cincinnati, Cincinnati, Ohio, United States of America
- Melissa A. Ashlock
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Current address: aTyr Pharma Inc., San Diego, California, United States of America
Affiliation Cystic Fibrosis Foundation, Bethesda, Maryland, United States of America
- Sarah E. Ernst
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Affiliation Department of Internal Medicine, University of Iowa, Iowa City, Iowa, United States of America
- Lijuan Fan
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Current address: Department of Medicine, Georgetown University, Washington, District of Columbia, United States of America
Affiliation Department of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America
- Douglas B. Hornick
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Affiliation Department of Internal Medicine, University of Iowa, Iowa City, Iowa, United States of America
- Philip H. Karp
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Affiliation Department of Internal Medicine, University of Iowa, Iowa City, Iowa, United States of America
- Umer Khan
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Affiliation Department of Biostatistics, Seattle Children’s Hospital, Seattle, Washington, United States of America
- James Lymp
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Affiliation Genentech, Inc., San Francisco, California, United States of America
- Alicia J. Ostmann
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Affiliation Department of Pediatrics, Cincinnati Children’s Hospital Medical Center and the University of Cincinnati, Cincinnati, Ohio, United States of America
- Amir Rezayat
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Affiliation Department of Pediatrics, Cincinnati Children’s Hospital Medical Center and the University of Cincinnati, Cincinnati, Ohio, United States of America
- Timothy D. Starner
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Affiliation Department of Pediatrics, University of Iowa, Iowa City, Iowa, United States of America
- Shajan P. Sugandha
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Affiliation Department of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America
- Hongtao Sun
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Affiliation Department of Pediatrics, Cincinnati Children’s Hospital Medical Center and the University of Cincinnati, Cincinnati, Ohio, United States of America
- Nancy Quinney
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Affiliation Department of Medicine, University of North Carolina, Chapel Hill, North Carolina, United States of America
- Scott H. Donaldson
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Affiliation Department of Medicine, University of North Carolina, Chapel Hill, North Carolina, United States of America
- Steven M. Rowe
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Affiliation Department of Medicine, University of Alabama at Birmingham, Birmingham, Alabama, United States of America
- Sherif E. Gabriel
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Affiliation N30 Pharmaceuticals, Aurora, Colorado, United States of America
Competing Interests
MAA owns Vertex stock. Dr. JL is currently employed at Genentech, Inc., South San Francisco, CA, USA, where final edits for this manuscript were performed. All original work was performed while at Seattle Children’s Research Institute. Dr. SEG is currently employed N30 Pharmaceuticals, Aurora, CO, USA, where final edits for this manuscript were performed. All original work was performed while at the University of North Carolina Medical Center. This does not alter the authors' adherence to all the PLOS ONE policies on sharing data and materials. All of the other authors have declared that no competing interests exist.
Author Contributions
Conceived and designed the experiments: JPC SHD SMR DBH TDS PHK MAA SEG. Performed the experiments: PHK SEE NLQ LF HS AJO SPS. Analyzed the data: JPC RDS UK JL AR SEG. Contributed reagents/materials/analysis tools: JPC RDS SMR BDH UK JL SEG. Wrote the manuscript: JPC RDS SHD SMR DBS UK JL HS MAA SEG.