About the Authors

Matthew L. Hirsch

mhirsch@email.unc.edu (MLH); rjs@med.unc.edu (RJS)

Affiliation Gene Therapy Center, University of North Carolina, Chapel Hill, North Carolina, United States of America

B. Matthew Fagan

Affiliation Human Embryonic Stem Cell Core Facility, University of North Carolina, Chapel Hill, North Carolina, United States of America

Raluca Dumitru

Affiliation Department of Cell and Developmental Biology, Neuroscience Center, University of North Carolina, Chapel Hill, North Carolina, United States of America

Jacquelyn J. Bower

Affiliation Department of Pathology and Laboratory Medicine, University of North Carolina, Chapel Hill, North Carolina, United States of America

Swati Yadav

Affiliation Gene Therapy Center, University of North Carolina, Chapel Hill, North Carolina, United States of America

Matthew H. Porteus

Affiliation Department of Pediatrics-Cancer Biology, Stanford University, Palo Alto, California, United States of America

Larysa H. Pevny

Affiliations Department of Genetics, University of North Carolina, Chapel Hill, North Carolina, United States of America, Department of Cell and Developmental Biology, Neuroscience Center, University of North Carolina, Chapel Hill, North Carolina, United States of America

R. Jude Samulski

mhirsch@email.unc.edu (MLH); rjs@med.unc.edu (RJS)

Affiliations Gene Therapy Center, University of North Carolina, Chapel Hill, North Carolina, United States of America, Department of Pharmacology, University of North Carolina, Chapel Hill, North Carolina, United States of America

Competing Interests

The authors have declared that no competing interests exist.

Author Contributions

Conceived and designed the experiments: MLH JJB MHP RJS LHP. Performed the experiments: MLH BMF RD JJB SY. Analyzed the data: MLH JJB MHP RJS. Contributed reagents/materials/analysis tools: MLH BMF JJB LHP RJS. Wrote the paper: MLH JJB MHP RJS.