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Absence of an Intron Splicing Silencer in Porcine Smn1 Intron 7 Confers Immunity to the Exon Skipping Mutation in Human SMN2
- Thomas Koed Doktor,
- Lisbeth Dahl Schrøder,
- Henriette Skovgaard Andersen,
- Sabrina Brøner,
- Anna Kitewska,
- Charlotte Brandt Sørensen,
- Brage Storstein Andresen
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- Published: June 3, 2014
- https://doi.org/10.1371/journal.pone.0098841