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Isofagomine In Vivo Effects in a Neuronopathic Gaucher Disease Mouse

  • Ying Sun,

    Affiliations The Division of Human Genetics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America, The Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America

  • Huimin Ran,

    Affiliations The Division of Human Genetics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America, The Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America

  • Benjamin Liou,

    Affiliations The Division of Human Genetics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America, The Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America

  • Brian Quinn,

    Affiliations The Division of Human Genetics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America, The Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America

  • Matt Zamzow,

    Affiliations The Division of Human Genetics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America, The Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America

  • Wujuan Zhang,

    Affiliations The Division of Pathology and Laboratory Medicine, Cincinnati Children's Hospital Medical Center, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America, The Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America

  • Jacek Bielawski,

    Affiliation The Department of Biochemistry and Molecular Biology, Medical University of South Carolina, Charleston, South Carolina, United States of America

  • Kazuyuki Kitatani,

    Affiliations The Department of Biochemistry and Molecular Biology, Medical University of South Carolina, Charleston, South Carolina, United States of America, The Department of Clinical Laboratory, Tottori University Hospital, Tottori University, Yonago, Japan

  • Kenneth D. R. Setchell,

    Affiliations The Division of Pathology and Laboratory Medicine, Cincinnati Children's Hospital Medical Center, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America, The Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America

  • Yusuf A. Hannun,

    Affiliation The Department of Biochemistry and Molecular Biology, Medical University of South Carolina, Charleston, South Carolina, United States of America

  • Gregory A. Grabowski

    Greg.Grabowski@cchmc.org

    Affiliations The Division of Human Genetics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America, The Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, Ohio, United States of America

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