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Long-Term Effect of Antibodies against Infused Alpha-Galactosidase A in Fabry Disease on Plasma and Urinary (lyso)Gb3 Reduction and Treatment Outcome
- Saskia M. Rombach,
- Johannes M. F. G. Aerts,
- Ben J. H. M. Poorthuis,
- Johanna E. M. Groener,
- Wilma Donker-Koopman,
- Erik Hendriks,
- Mina Mirzaian,
- Sijmen Kuiper,
- Frits A. Wijburg,
- Carla E. M. Hollak
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- Published: October 19, 2012
- https://doi.org/10.1371/journal.pone.0047805