About the Authors
- William E. Grose
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Affiliations Department of Pediatrics, The Ohio State University, Columbus, Ohio, United States of America, Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States of America
- K. Reed Clark
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Affiliations Department of Pediatrics, The Ohio State University, Columbus, Ohio, United States of America, Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States of America
- Danielle Griffin
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Affiliations Department of Pediatrics, The Ohio State University, Columbus, Ohio, United States of America, Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States of America
- Vinod Malik
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Affiliations Department of Pediatrics, The Ohio State University, Columbus, Ohio, United States of America, Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States of America
- Kimberly M. Shontz
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Affiliations Department of Pediatrics, The Ohio State University, Columbus, Ohio, United States of America, Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States of America
- Chrystal L. Montgomery
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Affiliations Department of Pediatrics, The Ohio State University, Columbus, Ohio, United States of America, Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States of America
- Sarah Lewis
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Affiliations Department of Pediatrics, The Ohio State University, Columbus, Ohio, United States of America, Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States of America
- Robert H. Brown Jr.
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Affiliation Department of Neurology, The University of Massachusetts Medical School, Worcester, Massachusetts, United States of America
- Paul M. L. Janssen
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Affiliation Department of Physiology and Cell Biology, The Ohio State University, Columbus, Ohio, United States of America
- Jerry R. Mendell
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* E-mail: Jerry.Mendell@nationwidechildrens.org (JRM); Louise.Rodino-Klapac@nationwidechildrens.org (LRRK)
Affiliations Department of Pediatrics, The Ohio State University, Columbus, Ohio, United States of America, Department of Neurology, The Ohio State University, Columbus, Ohio, United States of America, Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States of America
- Louise R. Rodino-Klapac
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* E-mail: Jerry.Mendell@nationwidechildrens.org (JRM); Louise.Rodino-Klapac@nationwidechildrens.org (LRRK)
Affiliations Department of Pediatrics, The Ohio State University, Columbus, Ohio, United States of America, Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, Ohio, United States of America
Competing Interests
The authors have declared that no competing interests exist.
Author Contributions
Conceived and designed the experiments: WEG JRM LRK. Performed the experiments: WEG KRC DG VM KMS CLM SL PMLJ LRK. Analyzed the data: WEG JRM LRK. Contributed reagents/materials/analysis tools: RHB. Wrote the paper: WEG JRM LRK.